What is NUC-1031 and its role in the treatment of advanced biliary tract cancer (aBTC)?
Label:chem
Topic
NUC-1031 is a phosphoramidate transformation of gemcitabine, a nucleoside analog used in cancer chemotherapy. It was developed to potentially improve the efficacy and safety profile of gemcitabine. The study discusses its evaluation in the phase III NuTide:121 trial for the treatment of advanced biliary tract cancer (aBTC).
Answer
NUC-1031 showed early promise in phase I trials with favorable safety and disease control in heavily pre-treated patients with solid tumors. However, in the phase III NuTide:121 trial, NUC-1031 combined with cisplatin did not improve overall survival compared to the standard gemcitabine/cisplatin regimen. It demonstrated a higher incidence of liver-related adverse events, leading to reduced treatment exposure and inferior overall survival. The study highlights the importance of thorough phase II evaluation before proceeding to phase III trials.
Return to Home
Chemical List
Knowledge you may be interested in